2,5-Dideoxy-2,5-imino-d-altritol as a new class of pharmacological chaperone for Fabry disease

Atsushi Kato*, Yukiko Yamashita, Shinpei Nakagawa, Yuriko Koike, Isao Adachi, Jackie Hollinshead, Robert J. Nash, Kyoko Ikeda, Naoki Asano

*Corresponding author for this work

Research output: Contribution to journalArticlepeer-review

37 Scopus citations

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Keyphrases

Pharmacology, Toxicology and Pharmaceutical Science